A 46-year-old woman with type 1 myotonic dystrophy (DM1) presented to the emergency department with dyspnea and palpitations.

DMD treatment SAT-3247 was safe and well-tolerated, and showed signs of increasing muscle strength in five adults, Satellos ...

gstt.sthames.nhs.uk Although bladder function is thought to be unaffected in Duchenne muscular dystrophy, 46/88 boys interviewed had urinary problems. Nine underwent video urodynamics, showing in ...

Delandistrogene moxeparvovec, a gene therapy for Duchenne muscular dystrophy (DMD), showed high dystrophin expression and a ...

Firefighters will be in Capitola Village this weekend, accepting donations on behalf of the Muscular Dystrophy Association ...

Acute myeloid leukemia (AML) can cause many different signs and symptoms. Some are more common with certain subtypes of AML. More often these symptoms are caused by something other than leukemia. But ...

Thirst, headache, and dry mouth are all signs it’s time to reach for water or a sports drink that’s low in sugar and high in electrolytes, says MedlinePlus. But the signs of dehydration aren ...

Dr. Binks brings 25 years of experience in clinical development and research, particularly in rare diseases and Duchenne muscular dystrophy (DMD). He has previously held key positions at Pfizer ...

“For nearly a decade, Sarepta has been a leader in advancing the treatment of Duchenne muscular dystrophy through innovative treatment options. With the approval of ELEVIDYS in Japan, children who are ...

May is ALS Awareness Month — an important cause to Stephanie Thompson. The Ottawa-based mom was in her early 40s when she began noticing the first signs of amyotrophic lateral sclerosis (ALS). The now ...

Peoples-Jones flashed enough potential to contend for Detroit’s WR3 role alongside Amon-Ra St. Brown and Jameson Williams, which prompted the Lions to re-sign him last offseason on a one-year ...

Earlier this year, Una Ennis took to social media with a heartfelt plea for funds so she could access specialist treatment abroad, following her seven-year-old son Archie’s muscular dystrophy ...