Researchers have identified how variations in a gene called TRIO can influence brain functions and result in distinct ...

Ankylosing spondylitis causes chronic back pain and joint fusion, affecting millions. Learn the early warning signs and what ...

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

Discover how cystic fibrosis genetics affect inheritance patterns and symptom. Learn about CFTR mutations, testing options, ...

The FDA granted rare pediatric disease designation for OCU410ST, a gene therapy designed to treat ABCA4-associated ...

Explore the evolving landscape of cell and gene therapies (CGTs) in gastroenterology. Key therapies include Anterogen's Cupistem and Takeda's Alofisel, the latter recently withdrawn by EMA. Understand ...

Gene delivery systems can target specific brain cells, a breakthrough that could lead to treatments for Parkinson's, ...

In medical breakthrough, a baby diagnosed with rare genetic disorder is thriving after customized CRISPR gene editing therapy ...

KJ Muldoon came into the world with a genetic time bomb ticking inside him.

Readers respond to an article about gene editing and object to cuts in research funding. Also: The Covid vaccine; Senator ...

Advancements in gene therapy for Duchenne muscular dystrophy (DMD) have improved the outlook for some patients, but further ...

Environmental factors such as lifestyle and the medications you take influence the effects your genes have on your body — and can clarify how diseases develop.