Ankylosing spondylitis causes chronic back pain and joint fusion, affecting millions. Learn the early warning signs and what ...

Preliminary data from ongoing Phase 1/2 trials show BEAM-302 is well tolerated and achieves dose-dependent, durable ...

The child will need to be monitored throughout his life, but researchers said the treatment’s success indicates that other ...

KJ Muldoon came into the world with a genetic time bomb ticking inside him.

Long considered a disease brought to the Americas by European colonizers, leprosy may actually have a much older history on ...

Researchers have identified how variations in a gene called TRIO can influence brain functions and result in distinct ...

Environmental factors such as lifestyle and the medications you take influence the effects your genes have on your body — and can clarify how diseases develop.

Doctors have successfully used gene-editing therapy to treat an infant born with a rare disorder. Experts believe the ...

Acute systemic infection caused the patient to develop fatal capillary leak syndrome, highlighting the unpredictability of ...

Genetic testing for hereditary cancer unexpectedly uncovered a case of myelodysplastic syndrome (MDS), highlighting the need ...

Doctors announced this week that they have treated a newborn baby with a rare genetic disease using the world’s first personalized gene editing therapy. Geoff Bennett discussed the treatment and its ...