Researchers developed an epigenetic editing approach to silence the PCSK9 gene, achieving long-term cholesterol reduction ...

Cell and gene therapies can be life-changing for patients with certain conditions, but the process of receiving them poses barriers for patients and caregivers that require multistakeholder solutions, ...

For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that must be delivered by injection three-to-six times each week.

Astellas has invested heavily in novel technologies that are not necessarily the most successful or popular in the industry.

the new investigation is intended to inform future clinical trials by including different dosages of the gene therapy, tests in male and female mice, and examinations in early- and late-onset ...

According to research by nova one advisor, the global cell and gene therapy market size was valued at $18.13 billion in 2023 ...

A new case report was published in Volume 16 of Oncotarget on February 5, 2025, titled “Acquired RUFY1-RET rearrangement as a ...

Gene editing technologies have been used to improve ... describes the company’s goal as reimagining the future of food. “The way that we’re approaching this is to unlock nature’s abilities ...