After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU.

Krystie Maddox, 12, who lives in Wolverhampton with her mother Molvia, 40, a business consultant and stepfather Mitchell, 34, also a consultant, has Friedreich's Ataxia, a rare inherited disorder ...

The Boston Celtics came into this season fully expecting to repeat as NBA champions. They brought back almost the same roster that they had a year ago. Even though they aren't the top seed in the ...

The Tribune, now published from Chandigarh, started publication on February 2, 1881, in Lahore (now in Pakistan). It was started by Sardar Dyal Singh Majithia, a public-spirited philanthropist ...

BOSTON (AP) — It’s been six months since Celtics star Jayson Tatum stood at center court in Boston’s TD Garden and addressed fans minutes after receiving his 2024 championship ring and watch ...

Disney fans return to the parks for reasons beyond the "magic," including new experiences and a sense of community. The immersive environment, from themed lands to dedicated cast members ...

Editor’s note: This is an automatically generated transcript. Please notify [email protected] if there are concerns regarding accuracy of the transcription. Patient advocacy organizations often ...

As a result, more repeat offenders are going to jail rather than merely receiving citations. Additionally, prosecutors have reported an uptick in felony charges for theft and drug offenses since ...

She didn’t see the gunman or hear the shots but knew what was happening. As a young man carried out a deadly shooting Thursday at Florida State University, Stephanie Horowitz looked out at the ...

STANFORD – It couldn’t have gone any better for the Stanford women’s rugby team. Playing on its home turf against rival Cal, the Cardinal earned its second consecutive USA Rugby Women’s D1 ...

CARLSBAD, Calif., April 21, 2025 (GLOBE NEWSWIRE) -- Design Therapeutics, Inc. (Nasdaq: DSGN), a clinical-stage biotechnology company developing treatments for serious degenerative genetic ...

DT-168 is a GeneTAC® small molecule, formulated as an eye drop, that is designed to selectively target the CTG repeat expansion in the TCF4 gene and reduce the expression of the mutant gene product ...