Biogen Canada Inc. is disappointed by INESSS's recommendation against listing SKYCLARYStm (omaveloxolone), despite its therapeutic potential for individuals living with Friedreich ataxia (FA) ? a ...

Biogen Canada Inc. is disappointed by INESSS's recommendation against listing SKYCLARYS™ (omaveloxolone), despite its therapeutic potential for individuals living with Friedreich ataxia (FA) — a ...

Initial Data from the Ongoing, Blinded Phase 1 Single-Ascending Dose Trial Has Demonstrated Favorable Safety and Pharmacokinetics IND Application Submitted to Expand RESTORE-FA Trial to U.S. Sites; ...

Researchers have developed a gene editing strategy that can repair the genetic problems that lead to Huntington's disease and Friedreich's ataxia. | Genetics And Genomics ...

Owen Donoghue, 44, took on the challenge to help eight-year-old Craigshill girl Ella-Rose Kennedy who has Friedreich ataxia – ...

A Columbia woman is putting a spotlight on a rare, degenerative disease, which targets the nervous system and often impairs ...

Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and Friedreich's ataxia.The ...

An Edmond family is on a mission to find a cure. For a decade, Michael Gehr has been battling Friedreich's ataxia, a rare ...

Flynn Mitchell said one the lowest moments of his life was trying to get home safely in his wheelchair in the middle of a ...

Billionaire Graeme Hart's granddaughter Jemima Hawkesby and her friend Flynn Mitchell graduating. She is fundraising to help ...

Scientists working at the NIH’s BRAIN Initiative have created new viral vectors that one day could lead to gene therapies for ...