“We are hosting the cure FA soiree on Saturday, June seventh At the Omni Hotel in Oklahoma City, and this event was born out ...

About DT-216P2 DT-216P2 is an improved formulation of a GeneTAC ® small molecule designed to specifically target the GAA repeat expansion mutation that is the underlying cause of FA and restore the ...

After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU.

Biogen’s Skyclarys is on course to becoming the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU after it was recommended by the EMA’s human ...

Biogen continues to be dedicated to advancing research and development efforts to enhance the understanding of FA and improve patient outcomes. This includes an ongoing, open-label, Phase 1 study to ...

Cash runway extended into 2028; capital proceeds to fund operations through potential 2027 efficacy readout for LX2006 in Friedreich ataxia cardiomyopathy Financing led by Frazier Life Sciences ...

Introduction: Friedreich ataxia (FA) is a monogenic recessive ataxia caused by reduction of a single mitochondrial protein, frataxin (FXN). Although the name of FA refers to the neurodegenerative ...

The kidney is the organ that filters blood and removes excess fluid and waste products, which are excreted in the urine. The kidney also has a role in the regulation of ion concentrations and ...

You may need to see a nephrologist if you have chronic kidney disease, kidney infections, or kidney failure. Nephrology is a specialty of internal medicine that focuses on treating diseases that ...