Friedreich’s ataxia (FA) is a neurodegenerative disease most people have never heard of, and it remains widely misunderstood ...

As with all products, we will keep its safety under close review. The Medicines and Healthcare products Regulatory Agency ...

When he was 19, he was halfway through a tattoo apprenticeship when he was diagnosed with Friedreich's Ataxia ... are affected by its life-altering symptoms. "The doctor told me that I had ...

But all that time, she had been reading up on my symptoms on the internet - and came across Friedreich's Ataxia. She was convinced that is what I had and, sure enough, when the results came back ...

Lexeo Therapeutics’ gene therapy provides a healthy version of the frataxin gene, which is critical for energy production in ...

Friedreich’s ataxia and more general forms of hereditary ataxias. The most common symptoms of the disease "are balance and walking difficulties, clumsiness, vision changes, speech difficulties ...

Stifel analysts said that Lexeo’s data showing reduced size and thickness of the heart’s left ventricle are “supportive of a drug effect” for the company’s gene therapy in Friedreich’s ataxia ...

Lexeo Therapeutics Inc. produced more positive interim data from early stage studies of its gene therapy to treat Friedreich’s ataxia cardiomyopathy. The results have prompted the company to continue ...

Biogen’s Skyclarys is on course to becoming the first approved medicine for the inherited neurological disease Friedreich’s ... that results in a range of symptoms that worsen over time ...

After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich ... a range of symptoms, including ...