News

Friedreich’s ataxia (FA) is a neurodegenerative disease most people have never heard of, and it remains widely misunderstood ...
Friedreich’s ataxia and more general forms of hereditary ataxias. The most common symptoms of the disease "are balance and walking difficulties, clumsiness, vision changes, speech difficulties ...
Considering taking supplements to treat friedreich ataxia? Below is a list of common natural remedies used to treat or reduce the symptoms of friedreich ataxia. Follow the links to read common ...
Lexeo Therapeutics’ gene therapy provides a healthy version of the frataxin gene, which is critical for energy production in ...
Discover how neuroimaging uncovers Friedreich ataxia progression patterns. Learn how biomarkers could transform clinical trials.
Stifel analysts said that Lexeo’s data showing reduced size and thickness of the heart’s left ventricle are “supportive of a drug effect” for the company’s gene therapy in Friedreich’s ataxia ...
A West Annapolis family has turned two life-altering diagnoses into more than $1 million for research toward finding a cure ...
Since reducing oxidative stress and mitochondrial dysfunction rather than reversing Friedreich's ataxia symptoms is the mechanism of action for vatiquinone, the agency might want more long-term ...
Biogen’s Skyclarys is on course to becoming the first approved medicine for the inherited neurological disease Friedreich’s ... that results in a range of symptoms that worsen over time ...
After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich ... a range of symptoms, including ...
Genetic analysis beyond the causative variants, and independent of the core clinical symptoms (pyramidal signs versus ataxia), might offer a more pertinent way to approach phenotypic variability.