News

Gene editing disrupts Huntington's mutation in mice
Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and ...
GEN - Genetic Engineering and Biotechnology News4d
Base Editors Curb Repeating DNA in Huntington’s and Ataxia Models
Early research shows that editing expanding trinucleotide repeats halts the lengthening process that causes neurological ...
Oppenheimer Predicts Up to ~550% Jump for These 2 ‘Strong Buy’ Stocks
After a rocky start to the spring, Wall Street came roaring back in May. President Trump’s softened tariff stance reignited ...
Oklahoma teenager uses love of music to find a cure for rare neurological disease
An Edmond family is on a mission to find a cure. For a decade, Michael Gehr has been battling Friedreich's ataxia, a rare ...
The Pharma Letter4d
Lexeo raises $80 million to shore up gene therapy work after layoffs
US biotech Lexeo Therapeutics has secured $80 million from a private placement, giving the company enough capital to push ...
Madras HC allows 28-week abortion for disabled rape survivor; says case ‘can brook no delay’
CHENNAI: A pregnant woman with 80% disability, who was raped by her neighbour, terminated her 28-week foetus on Tuesday after ...
pharmaphorum4d
Biogen’s Skyclarys is first EU drug for Friedreich’s ataxia
After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU.
Solid Biosciences to Participate at the Jefferies Global Healthcare Conference
Solid Biosciences Inc. (Nasdaq: SLDB) (the “Company” or “Solid”), a life sciences company developing precision genetic ...
pharmaphorum5d
CHMP backs Biogen’s Skyclarys for Friedreich’s ataxia
Biogen’s Skyclarys is on course to becoming the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU after it was recommended by the EMA’s human ...