Developed by Sarepta Therapeutics, Elevidys is a one-time, intravenous treatment that uses adeno-associated virus (AAV) ...

Gene therapy could be the newest breakthrough for Duchenne muscular dystrophy. While it may not be a cure, it can give independence to boys diagnosed with DMD.

Capricor Therapeutics is seeking FDA approval for CAP-1002, targeting heart function in Duchenne Muscular Dystrophy patients.

Italfarmaco's oral HDAC inhibitor Duvyzat has been recommended for approval in the EU as a treatment for Duchenne muscular dystrophy ... showed slower disease progression over 18 months of ...

There is no known cure for Duchenne muscular dystrophy and currently approved ... dogs raised hopes that CRISPR gene editing could halt progression of the disease in humans. Pfizer notes the ...

Tampa General Hospital (TGH) is raising the bar for heart care with the addition of two GE Healthcare Revolution APEX 512-Slice computed tomography (CT) scanners. The advanced scanners leverage ...

Taking center stage at the American Society of Gene and Cell Therapy meeting was the first-ever reported case of a ...

KalVista Pharmaceuticals, Inc. today announced that it will present new sebetralstat data at two upcoming congresses taking place concurrently from May 29?June 1, 2025: the 14th C1-inhibitor ...

New data demonstrated the benefits of Elevidys, a gene therapy for multiple Duchenne muscular dystrophy, in different age ...