Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular ...

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular ...

A number of strategies can help to ensure adequate joint care to best manage joint pain and stiffness in Duchenne muscular dystrophy (DMD).

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular dystrophy ...

Windsor musicians are set to join forces at a charity open mic night, raising funds to help young people living with a rare muscular disorder.

SKYN, the #1 non-latex condom brand in the world and U.S., proudly introduces SKYN KING, a premium line of large condoms crafted for superior comfort, confidence, and pleasure. Made with an advanced, ...

Designed to bring joy to kids with special needs and their families and caregivers, the third annual Double Good Days will take place June 8 at the Kohl Children's Museum in Glenview. Registration is ...

Apr. 8, 2025 — A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short ... at the a variant in gene SCN1B, which causes a severe form of developmental epileptic ...

Rocket Pharmaceuticals has shared early data from three patients that tie its gene therapy for an inherited heart disease to ...

Medera is a clinical-stage biopharmaceutical company focused on targeting difficult-to-treat and currently incurable diseases ...