Recent advances in biotechnology now provide a pathway to producing living human ... These could revolutionize medical research and drug development, greatly reducing the need for animal testing ...

Since the Orphan Drug Act went into effect in 1983, more than 600 drugs have been approved for rare diseases, according to ...

Researchers in pharma and beyond have historically glommed onto a limited number of disease targets, limiting innovation. AI ...

To have any impact, patient engagement needs to start with the drug development pathway, not at the point of licensing. That’s especially true in the rare disease space, where the unmet need is ...

The recent reductions in the US Food and Drug Administration’s workforce are poised to have a substantial impact on drug and biologic ...

Pharma needs to be mindful of all customers along the drug development pathway, from the outset, through the subsequent trials and regulatory processes, and on to delivery. Market research (MR ...

repurposed drug candidates that could reach patients sooner than traditional drug development pathways. About SOLVE FSHD SOLVE FSHD is a venture philanthropic organization established to catalyze ...