News

BioPharma Dive4h
Prasad’s FDA appointment pressures cell and gene therapy stocks
A vocal opponent of his predecessor Peter Marks, Vinay Prasad will now lead the office tasked with reviewing some genetic ...
GEN - Genetic Engineering and Biotechnology News5h
Getting the Right Gene Therapy to the Right Tissue
As we continue to see sequencing technologies advance and provide a deeper understanding of gene therapy targets along with ...
Analytics Insight15h
Transforming Cell and Gene Therapy Delivery with AI: Paving the Way for Personalized Medicine
Cell and gene therapies (CGTs) are revolutionizing the landscape of personalized medicine, offering treatments that were once ...
Fierce Healthcare1d
CMS will announce states participating in cell and gene therapy model—but health plans still have questions
In June, the Centers for Medicare & Medicaid Services (CMS) will name the participating states for the agency’s new Cell and ...
BioSpace8d
Cell and Gene Therapy Sector Enters ‘Critical’ Period After Marks’ FDA Exit
As tariffs, HHS workforce cuts and the ouster of CBER Director Peter Marks threaten the “lifeblood” of the cell and gene ...
Factor Bioscience to Present Non-Viral Gene Editing and Cell Engineering Innovations at the ASGCT Annual Meeting
Factor Bioscience Inc., a Cambridge-based biotechnology company focused on using its pioneering gene-editing platform to develop life-saving cell and gene therapies, today announced its participation ...
Forge Biologics Announces Eight Presentations at the American Society of Gene and Cell Therapy (ASGCT) 28th Annual Meeting
Forge Biologics ("Forge"), a leading manufacturer of genetic medicines and member of the Ajinomoto Bio-Pharma Services group, ...
Managed Healthcare Executive1d
Payers Express Low Confidence in Managing Cell and Gene Therapy Financial Risks
Plans expect cell and gene therapies to pose a moderate or major financial challenge in the next two to three years, ...
US FDA approves first cell-based gene therapy for rare genetic skin disorder
The U.S. Food and Drug Administration approved Abeona Therapeutics' gene therapy for a rare skin disorder on Tuesday.
“Unprecedented Recovery” – Gene Therapy Reverses Heart Failure in Breakthrough Study
A new gene therapy reversed heart failure in pigs by repairing heart function through cBIN1, showing major promise for future ...
Investigational gene therapy gives children with rare immune disorder a new lease on life
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...
Compact gene circuit uses microRNA to fine-tune therapy for rare diseases
Many diseases are caused by a missing or defective copy of a single gene. For decades, scientists have been working on gene ...