A gene editing drug custom-made for a critically ill baby showed that, for some ultra-rare diseases, it’s possible to design ...

Within hours of his birth last August, Baby KJ was so sick, his parents didn’t know if he’d live long enough to get to play with his three older siblings in Clifton Heights, just outside Philadelphia.

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a ...

Aldevron and Integrated DNA Technologies – both part of the Danaher Corporation – have achieved a medical milestone with the ...