Scientists are confident people with rare genetic diseases can be cured after the technology saved a baby's life.

Researchers at the University of California, Berkeley and the Children’s Hospital of Philadelphia worked together to test a ...

A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology ...

Ask scientists which gene-editing tool is most needed to advance gene therapy, and they'd probably describe a system that's ...

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

A newborn boy, KJ, was diagnosed at birth with a rare and potentially fatal genetic disease. He received a novel, on-demand CRISPR therapy in record time.

A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...

G ene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children's Hospital of ...