Epigenetic changes do not alter the genetic code itself, but by changing how DNA is organized within the cell, epigenetic ...

Intellia has leveraged its expertise in Crispr/Cas9 gene editing to advance a pipeline of in vivo and ex vivo therapies for diseases with high unmet medical needs. We believe Intellia's proprietary ...

Researchers at the Max Planck Institute for Evolutionary Anthropology have addressed a longstanding challenge in CRISPR ...

On May 12, 2025, the U.S. Court of Appeals for the Federal Circuit issued a long-awaited decision in Regents of the University of California v.

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

A study introduces a CRISPR model that predicts gRNA activity more accurately using chemically synthesized gRNAs. The model ...

Scientists have developed SMART (silently mutate and repair template), a strategy that dramatically expands the editable ...

Using the gene scissors CRISPR and stem cells, researchers at Stockholm University and the UK Dementia Research Institute (UK DRI) at King's College ...

A BABY has had his DNA rewritten to treat his a deadly genetic disorder in a world first. Little KJ Muldoon, now 15 months old, was diagnosed with an ultra rare disease just days after his birth, ...

With up to 40%, the point mutation H1069Q is the most common mutation of the Cu transporter ATPase7B in Western populations,” the authors wrote. “The aim of this study was to assess if a ...

Beam Therapeutics and Verve Therapeutics have each built their lead candidates on a technique billed as a safer alternative to conventional CRISPR. Clinical results ... was viewed mainly as a way to ...

A base-editing approach could also likely be a one-time treatment for all prion disease patients regardless of the genetic mutation causing ... the development of CRISPR-Cas9 gene editing in ...