KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

Beam Therapeutics rises after the FDA grants orphan drug status to its gene-editing therapy BEAM-101 for sickle cell disease.

For investors still seeking companiies with attractive long-term prospects, let's consider two in the biotech industry: ...

Thalassemia is passed down from parents to children. This means if one or both parents carry the gene, their child may be ...

Discover how gene editing and lab-grown meat are revolutionising healthcare and food in 2025, offering personalised ...

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

With gene therapy offering new hope for thalassemia, experts urge Indian govt to invest in early diagnosis, genetic testing, ...

Cell and gene therapy (C&GT) is set to revolutionise treatment of complex diseases, offering new possibilities for patients.

Thalassemia, a group of inherited blood disorders characterized by reduced or abnormal hemoglobin production, continues to ...

A four-year-old Pakistani girl diagnosed with severe thalassemia has been successfully treated with a Chinese-developed ...

KJ Muldoon came into the world with a genetic time bomb ticking inside him.