KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

Beam Therapeutics rises after the FDA grants orphan drug status to its gene-editing therapy BEAM-101 for sickle cell disease.

Early access via large-scale clinical study to establish the validity and utility of the FirstGene TM screen ...

For investors still seeking companiies with attractive long-term prospects, let's consider two in the biotech industry: ...

Thalassemia is passed down from parents to children. This means if one or both parents carry the gene, their child may be ...

Discover how gene editing and lab-grown meat are revolutionising healthcare and food in 2025, offering personalised ...

One of the most common signs of thalassemia is tiredness. Children may seem more tired than other kids, even after a good ...