Beta-thalassemia: Everyone has two beta globin genes (one on each chromosome 11). The severity depends on how many of these two genes are defective: One gene mutation: Beta-thalassemia minor ...

Geneticists have used a cutting-edge DNA base editing treatment on several patients to cure thalassemia, a prevalent and severe genetic blood disease.

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

With gene therapy offering new hope for thalassemia, experts urge Indian govt to invest in early diagnosis, genetic testing, ...

A new gene therapy developed at the Children's ... Nabeel was born with an inherited blood disorder called beta thalassemia. "It was just, like, so painful," she said. "Like I was in constant ...