Despite promising Phase 3 results, safety concerns, namely liver injury, have impacted Agios stock and could affect Pyrukund's approval and market adoption. Read the full report here.

A Thalassemia screening desk has been inaugurated at the NADRA centre in Sukkur on Saturday marking a significant step forwards the fight against the genetic disorder. The desk, established in ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent beta-thalassemia in August 2022, and exagamglogene autotemcel (exa-cel ...

for the treatment of adult patients with non-transfusion-dependent and transfusion-dependent alpha- or beta-thalassemia. The review classific CAMBRIDGE, Mass., Jan. 03, 2025 (GLOBE NEWSWIRE ...

Non-transfusion-dependent thalassemia encompasses three clinically distinct forms -- beta-thalassaemia intermedia, hemoglobin E/beta-thalassaemia (mild and moderate forms), and al ...

Bristol-Myers Squibb's Cobenfy launch shows strong initial sales and growth potential. Learn why BMY stock is a solid ...

Hence, we report an extremely rare presentation of PK deficiency hemolytic anemia with alpha thalassemia trait and CML. This patient is a 25-year-old male, resident of western India. He had presented ...

Allogene Therapeutics (ALLO) announced the publication of data from its Phase 1 ALPHA and ALPHA2 clinical studies of cemacabtagene ...

Moana 2 journeys into a Number 1 debut on the UK’s Official Film Chart. The sequel to 2016’s much-loved animated Disney film sails straight in at the top on digital downloads only, finishing ...

Kiss surges to No. 2 on Billboard's Hard Rock Digital Song Sales chart as “I Was Made For Lovin’ ... [+] You” matches the band's all-time peak on the ranking. Gene Simmons, Ace Frehley ...

At last silenced by the reality of the chart and the mess they company seem to have made of things. A pattern repeated over 5 years so the share value is less than the float price.