Stanford's CRISPR-TO tech enables precise RNA delivery in neurons, offering breakthrough treatment potential for ALS, spinal injuries, and neurodegenerative diseases.

He’s among the first to be successfully treated with a custom therapy that seeks to fix a tiny but critical error in his ...

In a stunning medical breakthrough that effectively brings designer babies out of the realm of science fiction, a ...

STAT reporters chat about the mood in the gene editing field, M&A deals in biotech, and leadership changes at Novo Nordisk.

Researchers at the National University of Singapore (NUS) have developed a scalable, non-viral technology that efficiently ...

Beam Therapeutics CEO John Evans warns against AI hype in drug development, drawing parallels to past CRISPR expectations, ...

A “genetic surgery” or “interventional genetics” system for individualized treatments would be a marriage of drug development ...

Research teams funded by the National Institutes of Health (NIH) have created a versatile set of gene delivery systems that can reach different neural cell types in the human brain and spinal cord ...

Currently, the researchers are using CRISPR-TO to move endogenous RNAs – RNA molecules that are naturally produced within the ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene-editing treatment made just for him. Researchers described the case in a new study, say ...

Discover how scientists essentially added a guide molecule to the gene editor to help it insert an entire gene into the most ...