Norah Awad has lived with beta thalassemia major, a severe blood disorder that has required monthly transfusions since she ...

While gene therapy has emerged as a promising alternative for treating beta-thalassemia ... pointing out that better HLA typing is a major reason. However, a "big quantum leap" was the marked ...

It’s back to the drawing board for bluebird bio and its discussions with NICE, which has rejected its beta thalassaemia gene therapy Zynteglo for regular NHS use in first draft guidance.

LentiGlobin BB305 aims to treat beta-thalassemia major and severe sickle cell disease ... a single treatment of the gene therapy corrected the main genetic defect which causes the condition.

Thalassemia and sickle cell anaemia are common genetic disorders in India. Early testing, prenatal screening, and improved ...

India has around 50 million (5 crore) carriers of the ß (beta) thalassemia trait ... U.S. has shown promising results for gene therapy for thalassemia major. • FDA-Approved Therapies: Trials ...

the first CRISPR/Cas9 gene-editing therapy in the UAE. This achievement opens new horizons and offers innovative treatment for patients suffering from sickle cell disease (SCD) and transfusion ...

Thalassemia and Sickle Cell Anaemia are common genetic disorders, with options for treatment and prevention available.