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Belfast News Letter on MSN5h
Student takes on Belfast Abseil in memory of her Nana
Emma Adair, 22, a student from Crumlin abseiled 120ft down the Europa Hotel in Belfast for charity. But her challenge doesn’t ...
Morning Call PA27d
Patient dies following muscular dystrophy gene therapy, Sarepta reports
WASHINGTON (AP) — Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy ... A Lehigh Valley high school student studied ...
Setback in gene therapy for Duchenne muscular dystrophy as immune system emerges as key barrier
A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...
Charity Today10d
Charity hosts FREE event for people with neuromuscular conditions
The Information Day takes place on Wednesday, 4 June 2025, in Lisburn, Co. Antrim, and is organised by the leading charity ...
Business Wire1mon
Italfarmaco Provides Overview on Givinostat as Treatment for Duchenne Muscular Dystrophy: Progress in Global Access, Regulatory Milestones and Clinical Trials
About Duchenne Muscular Dystrophy DMD is a progressive neuromuscular disorder caused by a mutation in the DMD gene which affects the production of a protein called dystrophin. 3 Dystrophin is a ...
WFMZ-TV27d
Patient dies following muscular dystrophy gene therapy, Sarepta reports
FILE - A sign for the U.S. Food and Drug Administration ... died while taking its closely watched gene therapy for muscular dystrophy, sending company shares plummeting more than 25%.