A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology ...

PHILADELPHIA (WPVI) -- An infant, who was born with a deadly disease, is now thriving, thanks to a medical first performed at ...

KJ Muldoon became the first patient to undergo personalized CRISPR treatment, a therapy that found the one uniquely mutated gene out of 20,000 in his little body, and fixed it.

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can ...

The baby, KJ, was born with severe CPS1 deficiency, a rare genetic condition that affects only one in 1.3 million people.

G ene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

Toto, I have a feeling we’re not in Philadelphia anymore. On Thursday, St. Christopher’s Hospital for Children hosted a ...

PHILADELPHIA, May 6, 2025 /PRNewswire/ -- Researchers at Children's Hospital of Philadelphia (CHOP ... and her team have previously found that most familial cases are linked to the ALK mutation ...

News broke yesterday that researchers in Philadelphia appear to have successfully treated a 6-month-old baby boy, called KJ, ...

Scientists sprinted to create personalized medicine for baby KJ powered by CRISPR, a powerful gene-editing technology that ...