News

Cape Cod Times1d
Falmouth teen begins human gene therapy for sickle cell. 'High risk and it's scary'
A Falmouth teen, Jayden Wilsey, is the first to receive gene therapy to treat sickle cell at Boston Children's Hospital.
Sickle Cell Disease News19h
Oral inhibitor rilzabrutinib granted FDA orphan drug status for SCD
The FDA has granted orphan drug status to rilzabrutinib, an investigational therapy to prevent pain crises in sickle cell ...
Sickle Cell Disease News3d
Malaria prevention is crucial to sickle cell disease management
Columnist Oluwatosin Adesoye explains why preventing malaria infections is particularly important for those with sickle cell ...
WGAL on MSN3d
Woman accused of faking sickle cell anemia to steal $560K in hospital care in Lancaster County
A New Jersey woman stole $560,000 in hospital treatments by pretending she had sickle cell anemia, according to the Lancaster County district attorney. Taleah McKnight, 30, is charged with theft by ...
Beam Therapeutics Announces U.S. FDA Orphan Drug Designation Granted to BEAM-101 for the Treatment of Sickle Cell Disease
Beam Therapeutics Inc. (Nasdaq: BEAM), a biotechnology company developing precision genetic medicines through base editing, ...
PharmiWeb3d
Sanofi's Rilzabrutinib Gains Orphan Drug Designation for Sickle Cell Disease in the US
Sanofi announced today that the U.S. FDA has granted orphan drug designation to rilzabrutinib for the treatment of sickle ...