Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

Exagamglogene autotemcel (exa-cel) (Casgevy®) is a gene therapy for treating sickle cell disease in patients 12 years and older with recurrent vaso-occlusive crises and transfustion-dependent beta ...

Chow is City of Hope’s first sickle cell patient, while a beta thalassemia patient has been treated at Children’s National. Several authorized centers told WIRED they will begin infusions of ...

Thalassemia is an inherited disease that ... symptoms thalassemia major or Cooley anemia changes on two beta-globin genes sickle trait and changes in the beta-globin gene coinheritance changes ...

"We have about eight patients that are in the insurance approval process," she said, for gene therapy treatments for beta thalassemia and sickle cell disease. "It's something that we do expect to ...

A three-year study by Metropolis Healthcare reveals that 28.4 per cent of nearly 20,000 children screened for ...

A new study reveals that over one in four Indian children under 12 carry inherited blood disorders. The findings highlight ...