Hosted on MSN1mon
CRISPR therapy corrects muscular dystrophy mutations and regrows muscles in mice
The researchers note this therapy is not a complete ... In the case of limb-girdle muscular dystrophy, muscle deterioration is progressive and young adults lose the ability to walk and normal ...
pharmaphorum7d
Sanofi wagers $400m on miRecule muscular dystrophy therapy
Sanofi has added to its rare disease pipeline by licensing an antibody-RNA conjugate (ARC) for facioscapulohumeral muscular dystrophy (FSHD ... a "best-in-class therapy designed to suppress ...
The EMBO Journal9d
Type-2 innate signals are dispensable for skeletal muscle regeneration and pathology linked to Duchenne muscular dystrophy
Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...
Business Wire1mon
FDA Grants Orphan Drug Designation to IPS HEART’s GIVI-MPC Stem Cell Therapy for Becker Muscular Dystrophy
a human iPSC-derived cardiac therapy for treatment of Duchenne cardiomyopathy and heart failure that develops new heart muscle. About Becker & Duchenne Muscular Dystrophy BMD is a muscular disease ...
BioWorld29d
Ips Heart’s stem cell therapy designated orphan drug for Becker muscular dystrophy
Ips Heart Inc. has been awarded orphan drug designation by the FDA for its GIVI-MPC stem cell therapy for Becker muscular dystrophy. GIVI-MPC has the unique ability to create new muscle with full ...