Non-transfusion-dependent thalassemia encompasses three clinically distinct forms -- beta-thalassaemia intermedia, hemoglobin E/beta-thalassaemia (mild and moderate forms), and al ...

Hemoglobin is the iron-rich protein ... and some people with this type may require occasional treatments (e.g., blood ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

You probably had a hemoglobin electrophoresis test done at some point to make the diagnosis of beta thalassemia minor, so this would be useful to present to new doctors. Making a definitive ...

I owe my long interest in inherited blood diseases and tropical medicine to a series of characteristically bizarre decisions by the British Army. In 1958, 2 years after qualifying in medicine from ...

Beta-thalassemia is a rare blood disorder caused by a genetic defect in hemoglobin. Several manufacturers are developing novel treatments for the disease, including Vertex, which has partnered ...

There were no serious adverse events or treatment-related mortalities. Evidence Rating Level: 2 (Good) Study Rundown: ...