News

Medscape2h
Italian Duchenne Muscular Dystrophy Drug Gets Okayed in Europe
The CHMP recommends conditional marketing authorization for Duvyzat to treat Duchenne muscular dystrophy in patients aged 6 ...
STAT1d
Capricor Therapeutics forges ahead with FDA on Duchenne drug, despite political tumult
While there have been reports from drugmakers about possible interruptions with FDA matters due to staff layoffs, one company ...
9-year-old boy with Duchenne muscular dystrophy surprised with new van
A community has come together to surprise 9-year-old Killian Bauer who is living with Duchenne muscular dystrophy, with a ...
Healio7d
VIDEO: Latest treatment options in Duchenne muscular dystrophy
John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the latest treatment advancements for Duchenne muscular dystrophy.
The American Journal of Managed Care11d
At-Home DMD Video Assessment Found Valid, Reliable
The remote measurement tool enables Duchenne muscular dystrophy (DMD) assessments through analysis of caregiver-recorded ...
My son has Duchenne muscular dystrophy. Screening babies would help | Column
Newborn screening is also cost-effective. Testing that takes just a few dollars per baby can save families and the health ...
The Manila Times1d
Solid Biosciences to Present at the American Society of Gene and Cell Therapy's 28th Annual Meeting
Solid Biosciences Inc. (Nasdaq: SLDB), a life sciences company developing precision genetic medicines for neuromuscular and ...
Yahoo Finance6d
Dyne Therapeutics Receives European Medicines Agency (EMA) Orphan Drug Designation for DYNE-251 in Duchenne Muscular Dystrophy
April 24, 2025 (GLOBE NEWSWIRE) -- Dyne Therapeutics, Inc. (Nasdaq: DYN), a clinical-stage company focused ... DYNE-251 for the treatment of Duchenne muscular dystrophy (DMD).