A Falmouth teen, Jayden Wilsey, is the first to receive gene therapy to treat sickle cell at Boston Children's Hospital.

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

By reprogramming brain cells, a new gene therapy approach for Alzheimer's developed by UC San Diego researchers could address ...

While heritable human genome editing is banned in the United States, across Europe and much of the world, the technology ...

The Platform Technology Designation, which precedes the current FDA leadership, is designed to streamline the drug ...

Cell and gene therapy (CGT) represents the pinnacle of biomedical innovation, offering unprecedented potential to treat, ...

Machine learning models have seeped into the fabric of our lives, from curating playlists to explaining hard concepts in a ...

This first-in-human trial is testing a highly unconventional method: delivering fat-derived stem cells from the patient ...

Researchers have identified an early postnatal window that allows gene transfer to circulating blood stem cells, advancing ...

Interim results from a small group of children in a Phase I/II trial are essentially in line with that of Elevidys, according ...

Scientists at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, have found that gene editing using ...

Unlike existing treatments for Alzheimer’s that target unhealthy protein deposits, the new approach developed at UC San Diego ...