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PharmiWeb3d
Gene Therapy Market Anticipated to Witness 20% CAGR Growth by 2029: Top Key Players like Novartis, Roche, CRISPR Therapeutics
The global gene therapy market is projected to grow at a significant CAGR of 20% from 2024 to 2029. This growth is driven by ...
Stocktwits on MSN17h
uniQure Stock Jumps On FDA’s Breakthrough Therapy Designation For Investigational Gene Therapy: Retail’s Optimistic
Shares of gene therapy developer uniQure N.V. (QURE) shot up 41% on Thursday afternoon after it announced that the U.S. Food ...
uniQure Announces FDA Breakthrough Therapy Designation Granted to AMT-130 for the Treatment of Huntington’s Disease
Breakthrough Therapy designation based on clinical evidence from Phase I/II trials showing meaningful slowing of disease progression ~~ ...
EurekAlert!10d
Breakthrough gene therapy offers hope for rare, deadly heart disease in young men
A team at CNIC has developed an innovative gene therapy to treat arrhythmogenic right ventricular cardiomyopathy type 5 ...
Muscular Dystrophy News21h
FDA OKs trial of SRP-9005 gene therapy for LGMD type 2C
The FDA cleared Sarepta to start dosing in a first-in-human clinical trial testing the gene therapy SRP-9005 in people with ...
Taiwan News13h
Europe CRISPR Gene Editing Market (CAGR) projected at 27.3%, Cultural Exploration Ethnography’s Influence on Consumer Insights
Market Overview: The European CRISPR gene editing market has experienced significant expansion, driven by advancements in biotechnology and increasing investment in genetic research. With a compound ...
Atsena Therapeutics Granted U.S. FDA Regenerative Medicine Advanced Therapy Designation for ATSN-201 Gene Therapy to Treat X-linked Retinoschisis
Atsena Therapeutics, a clinical-stage gene therapy company focused on using the life-changing power of genetic medicine to reverse or prevent blindness, today announced that the U.S. Food and Drug ...
Precision Medicine Online7d
Opus Genetics Eyes 2026 Start for Pivotal Trial of Gene Therapy for Rare Retinal Disease
On the heels of its acquisition by Ocuphire Pharma, Opus is planning next steps for its Leber congenital amaurosis type 5 ...
PharmiWeb8d
Plasmid DNA Manufacturing Market Analysis: Trends, Opportunities, and Forecast
R&D Grade: Primarily utilized in preclinical studies and research applications, this segment plays a crucial role in the early stages of therapeutic development. Cell & Gene Therapy: This segment held ...