A TERMINALLY-ill chef has vowed to run her 600th marathon by the summer. Doctors diagnosed Brenda O’Keeffe, 48, from Co Cavan, with a rare and untreatable type of bone marrow cancer last year. The ...
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What Is Amyloidosis?
Amyloidosis is a rare protein-related condition that occurs when your body produces too many amyloid proteins, causing damage to your organs and tissues. Amyloid proteins are a type of protein ...
Amyloidosis occurs due to a buildup of amyloid proteins in the body. Along with treatment, complementary therapy can help with symptoms. Some examples include movements, such as yoga, sleep ...
Chiefs Hall of Honor member Art Still is a proud foot soldier in the Amyloidosis Army, a nonprofit he started hoping to ...
Immix Biopharma (IMMX) announced that the U.S. FDA has granted RMAT designation to sterically-optimized CAR-T NXC-201 for the treatment of ...
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Role of Genes in hATTR Amyloidosis
Hereditary ATTR amyloidosis (hATTR amyloidosis) is a rare, debilitating disease that runs in families. It's caused by ...
While healthy transthyretin moves hormones through blood and spinal fluid, misfolded versions of the protein form dangerous clumps in the heart and along nerves-triggering a progressive and fatal ...
Alnylam’s (ALNY) treatment of transthyretin-mediated amyloidosis, or ATTR amyloidosis, was granted FDA orphan designation, according to a post ...
Amvuttra (vutrisiran) is a follow-up to Alnylam's earlier RNA interference (RNAi) ATTR amyloidosis therapy Onpattro (patisiran), which was cleared by NICE for NHS use in 2019, but offers a simpler ...