The European Medicines Agency (EMA) has designated allopurinol as the first orphan drug for the treatment of Marfan syndrome, ...

Eton Pharmaceuticals is able to buy orphan drugs from large pharma companies, where they are too small to matter. Read why ...

U.S. drugmakers are charging significantly more for new treatments, particularly those targeting rare diseases, as the median ...

Under the Medicare Drug Price Negotiation Program, the HHS secretary negotiates directly with manufacturers on the prices ...

Prices of newly launched drugs in the U.S. have more than doubled from 2021 to 2024, driven by rare disease therapies, ...

Kuick Research Report Gives Detailed Insight On More Than 1400 FDA Orphan Designated Drugs And Highlights More Than USD 190 ...

EMA grants orphan drug designation to Quoin Pharma’s QRX003 for the treatment of Netherton syndrome: Ashburn, Virginia Thursday, May 22, 2025, 15:00 Hrs [IST] Quoin Pharmaceutic ...

Evotec's insights into GPCRs and waveRAPID technology reveal new opportunities in drug discovery, focusing on orphan ...

U.S. prices for new drugs more than doubled last year compared to 2021, as companies developed more therapies for rare ...

The European Medicines Agency (EMA) has designated allopurinol as the first orphan drug for the treatment of Marfan syndrome, ...

The European Medicines Agency (EMA) has designated allopurinol as the first orphan drug for the treatment of Marfan syndrome, ...